Valdes, P.Colin, P.Gaudry, J. P.Aebi, A.Schneider, B. L.2023-01-302023-01-302023-01-302022-12-01https://infoscience.epfl.ch/handle/20.500.14299/194364WOS:000899950600277Biotechnology & Applied MicrobiologyGenetics & HeredityMedicine, Research & ExperimentalResearch & Experimental MedicineGene therapy against amyotrophic lateral sclerosis: a bicistronic AAV vector for RNAi against mutated SOD1text::conference output::conference proceedings::conference paper