Cas9/gRNAs Selective Targeting of the Beethoven Tmc-1 Mutant Allele for Treating Progressive Hearing Loss by AAV-Based Delivery

Solanes, PaolaPan, BifengAebischer, PatrickHolt, Jeffrey R.Schneider, Bernard2018-12-132018-12-132018-12-132018-05-01https://infoscience.epfl.ch/handle/20.500.14299/152341WOS:000435342201165Biotechnology & Applied MicrobiologyGenetics & HeredityMedicine, Research & ExperimentalBiotechnology & Applied MicrobiologyGenetics & HeredityResearch & Experimental MedicineCas9/gRNAs Selective Targeting of the Beethoven Tmc-1 Mutant Allele for Treating Progressive Hearing Loss by AAV-Based Deliverytext::conference output::conference proceedings::conference paper