Allele-specific gene disruption through discrimination of a single base change by S. aureus Cas9-KKH prevents progressive hearing loss after AAV-mediated gene delivery

Gyorgy, B.Nist-Lund, C.Pan, B.Asai, Y.Karavitaki, K. D.Kleinstiver, B. P.Garcia, S. P.Zaborowski, M. P.Solanes, P.Spataro, S.Schneider, B. L.Joung, J. K.Geleoc, G. S. G.Holt, J. R.Corey, D. P.2019-12-122019-12-122019-12-122019-11-01https://infoscience.epfl.ch/handle/20.500.14299/163954WOS:000495173100028Biotechnology & Applied MicrobiologyGenetics & HeredityMedicine, Research & ExperimentalResearch & Experimental MedicineAllele-specific gene disruption through discrimination of a single base change by S. aureus Cas9-KKH prevents progressive hearing loss after AAV-mediated gene deliverytext::conference output::conference proceedings::conference paper